Looking for a cure
Duchenne Muscular Dystrophy (DMD) is a devastating muscle-wasting disease. It is the most common and severe form of Muscular Dystrophy. Diagnosed in childhood, it mainly affects boys and there is currently no cure.
Started by families affected by the disease, Duchenne UK has one clear aim – to end Duchenne.
Duchenne UK fund research that’s focused on getting treatments to those affected – as well as pushing for an effective treatment in the future. By connecting leading researchers within the industry, the NHS and patients, Duchenne UK challenge every stage of drug development, from research, clinical trials and drug approval. Not only this, Duchenne UK connect families with each other to create a network of mutual support and to pool resources, knowledge and experiences together.
Why It Matters:
There is currently no cure for Duchenne Muscular Dystrophy. Funding research that’s focused on getting treatments to those affected, as well as pushing for effective treatment in the future is essential. For children with DMD, muscle weakness starts in early childhood and men and women with the disease have a reduced life expectancy and will not live beyond their 40s.
Advances in research and knowledge of the disease are increasing life expectancy. Now, more and more young adults with DMD are leading full lives – going to university, having relationships, and living independently. Uncovering new treatments, delivering clinical trials and connecting families will ensure we are able to focus on ending Duchenne as quickly and effectively as possible.